Highlights ■ LATAM RegistrAME is the first clinical registry study of spinal muscular atrophy linked to 5q-SMA in Latin America (LATAM), including all ages. ■ This study will provide the first clinical evidence of access to medication for 5q-SMA treatment in LATAM. ■ It will describe the functional assessment and ventilatory support of 5q-SMA patients with diverse sociodemographic aspects. ABSTRACT Spinal muscular atrophy is a rare hereditary neurodegenerative disease characterized by  progressive motor neuron loss. The most common form of […]