TY - JOUR T1 - Longitudinal data collection in pediatric and adult patients with 5q spinal muscular atrophy in Latin America: LATAM RegistrAME study – a clinical registry study protocol A1 - Batista, Elice Carneiro A1 - Zanoteli, Edmar A1 - Monfardini, Frederico A1 - Santos, Gustavo Prado dos A1 - Silva, Gisele Sampaio A1 - Berwanger, Otávio A1 - Rizzo, Luiz Vicente A1 - Fonseca, Henrique Andrade Rodrigues da Y1 - 2024/11/13/ KW - Muscular atrophy KW - spine KW - 5q-SMA KW - Rare disease KW - Motor milestone PY - 2024 DO - 10.31744/einstein_journal/2024AE1133 JF - einstein (São Paulo) VL - 22 SP - EP - LA - en SN - 1679-4508 UR - https://journal.einstein.br/article/longitudinal-data-collection-in-pediatric-and-adult-patients-with-5q-spinal-muscular-atrophy-in-latin-america-latam-registrame-study-a-clinical-registry-study-protocol/ Y2 - 2026/05/19/03:31:03 ER -